Zolgensma: Marley gets 'miracle drug' for rare disorder

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Boy with rare genetic condition received NHS treatment using a 'miracle drug', his parents say

The British Medical Journal has said it isMs Walton said it had been a "rollercoaster" experience since it was licensed while they waited to find out if their son was eligible.

Their son's condition causes muscle weakness and affects movement and breathing, meaning most babies who have it do not live past two years without intervention.The money raised for Marley will be used for continuing treatment including private physiotherapy and equipment, his family said.

 

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Sadly price of £1.79m so will be can't afford treatment for a lot. As NI put up to fund NHS one wonders the reason we need to increase funding. More expensive treatments approved?

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