CEO Vas Narasimhan of Swiss drugmaker Novartis. Novartis' AveXis unit just got a new treatment approved in the US.Called Zolgensma, it is a type of cutting-edge, one-time treatment called a"gene therapy" that treats the disease spinal muscular atrophy at its genetic root.
That means it should work longer than the typical drug, but has also translated to a much higher price tag, too.Visit Business Insider's homepage for more storiesThe FDA just approved a cutting-edge new treatment for a devastating rare genetic disease called spinal muscular atrophy. The treatment, Novartis's Zolgensma, is a one-time therapy that works to treat the disease at the genetic level. That meants the drug's effects should last for a long time, though it's still not known if the treatment will be permanent.
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